Specialized delivery systems for genetic medicines

The circular graphic at its center shows a wide range of therapeutic cargos that are used in genetic medicine, including small interfering RNA (siRNA), antisense oligonucleotides (ASOs), messenger RNA (mRNA), DNA, and gene editing tools. These cargos hold promise of fundamentally changing how we treat diseases by targeting their root causes, not the symptoms. Effective treatment depends on transporting these genetic materials inside cells, a challenge that is currently being addressed with some of the delivery methods described.

In the ring surrounding the center are delivery systems that can be used as carriers for the cargos and the outer ring contains comments on the delivery systems.

GoldenNeuro is focused on creating next-generation genetic therapies by refining both the therapeutic cargos and the delivery technologies to align with the needs of a particular disease target.